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Onasemnogene Abeparvovec as New Gene Therapy in Patients with Spinal Muscular Atrophy – a Review of the Literature Cover

Onasemnogene Abeparvovec as New Gene Therapy in Patients with Spinal Muscular Atrophy – a Review of the Literature

Open Access
|Sep 2021

References

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Language: English
Page range: 85 - 100
Published on: Sep 22, 2021
Published by: SAN University
In partnership with: Paradigm Publishing Services
Publication frequency: 1 issue per year

© 2021 Gabriela Ręka, Angelika Pawlak, Halina Piecewicz-Szczęsna, published by SAN University
This work is licensed under the Creative Commons Attribution-ShareAlike 3.0 License.